Protocol for initiation of miglustat treatment in NP-C. Reproduced

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Last updated 21 setembro 2024
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Distinct Niemann-Pick Disease Type C Clinical, Cytological, and Biochemical Phenotype in an Adult Patient With 1 Mutated, Overexpressed NPC1 Allele - Julia Jecel, Klaus Harzer, Eduard Paschke, Stefanie Beck-Wödl, Peter Bauer, Milos
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Severely impaired CTL killing is a feature of the neurological disorder Niemann-Pick disease type C1 - ScienceDirect
Protocol for initiation of miglustat treatment in NP-C. Reproduced
IJMS, Free Full-Text
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Protocol for initiation of miglustat treatment in NP-C. Reproduced with
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Different Niemann-Pick C1 Genotypes Generate Protein Phenotypes that Vary in their Intracellular Processing, Trafficking and Localization
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Tolerance of chronic HDACi treatment for neurological, visceral and lung Niemann-Pick Type C disease in mice
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Full article: New therapies in the management of Niemann-Pick type C disease: clinical utility of miglustat
Protocol for initiation of miglustat treatment in NP-C. Reproduced
MRx Pipeline October by Magellan Rx Management - Issuu
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study - The Lancet Neurology
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Loss of NPC1 enhances phagocytic uptake and impairs lipid trafficking in microglia
Protocol for initiation of miglustat treatment in NP-C. Reproduced
Frontiers Adult-Onset Niemann–Pick Disease Type C: Rapid Treatment Initiation Advised but Early Diagnosis Remains Difficult

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