Niemann-Pick Disease Type C Archives - The Children's Inn at NIH

Gene therapy shows promise for treating Niemann-Pick disease type C1

Timeline – 2010-2017 - The Children's Inn at NIH

Niemann-Pick Disease Type C1: The NIH Clinical Center Audiology Unit's Progress

Niemann-Pick Disease

Volunteer Story: Victoria and Julia (Niemann-Pick Disease Type C)

Miglustat, C10H21NO4

Timeline – 2010-2017 - The Children's Inn at NIH

Download - United Way of Central Maryland

Institute of child health hi-res stock photography and images - Alamy

Niemann-Pick disease type C

National Niemann-Pick Disease Foundation, Inc. - October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to www.nnpdf.org

Niemann-Pick disease type C as a neurovisceral disease. Schematic

Spectrum of Movement Disorders in Niemann-Pick Disease Type C - Tremor and Other Hyperkinetic Movements

Prenatal-Onset Niemann–Pick Type C Disease with Nonimmune Hydrops Fetalis - ScienceDirect

Two-Year-Old Kamryn Living with Niemann-Pick Disease Type C (NPC) - The Children's Inn at NIH